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Academic Journal

Short 2'-O-methyl/LNA oligomers as highly-selective inhibitors of miRNA production in vitro and in vivo.

  • Authors : Koralewska N; Department of Molecular and Systems Biology, Institute of Bioorganic Chemistry, Polish Academy of Sciences, Poznan 61-704, Poland.; Corradi E

Subjects: MicroRNAs*/MicroRNAs*/MicroRNAs*/genetics ; MicroRNAs*/MicroRNAs*/MicroRNAs*/metabolism ; Oligonucleotides*/Oligonucleotides*/Oligonucleotides*/chemistry

  • Source: Nucleic acids research [Nucleic Acids Res] 2024 Jun 10; Vol. 52 (10), pp. 5804-5824.Publisher: Oxford University Press Country of Publication: England NLM ID: 0411011 Publication Model: Print Cited Medium: Internet ISSN:

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Academic Journal

Site-specific N-alkylation of DNA oligonucleotide nucleobases by DNAzyme-catalyzed reductive amination.

  • Authors : Boyd RD; Department of Chemistry, University of Illinois Urbana-Champaign, 600 South Mathews Avenue, Urbana, IL 61801, USA.; Kennebeck MM

Subjects: DNA, Catalytic*/DNA, Catalytic*/DNA, Catalytic*/chemistry ; DNA, Catalytic*/DNA, Catalytic*/DNA, Catalytic*/metabolism ; Oligonucleotides*/Oligonucleotides*/Oligonucleotides*/chemistry

  • Source: Nucleic acids research [Nucleic Acids Res] 2024 Aug 27; Vol. 52 (15), pp. 8702-8716.Publisher: Oxford University Press Country of Publication: England NLM ID: 0411011 Publication Model: Print Cited Medium: Internet ISSN:

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Academic Journal

Unveiling the adverse events of Nusinersen in spinal muscular atrophy management based on FAERS database.

  • Authors : Jiang Y; Mental Health Center of Jiangnan University, Wuxi Central Rehabilitation Hospital, Wuxi, Jiangsu, 214151, China.; Shen Y

Subjects: Oligonucleotides*/Oligonucleotides*/Oligonucleotides*/adverse effects ; Oligonucleotides*/Oligonucleotides*/Oligonucleotides*/therapeutic use ; Muscular Atrophy, Spinal*/Muscular Atrophy, Spinal*/Muscular Atrophy, Spinal*/drug therapy

  • Source: Scientific reports [Sci Rep] 2024 Jul 25; Vol. 14 (1), pp. 17138. Date of Electronic Publication: 2024 Jul 25.Publisher: Nature Publishing Group Country of Publication: England NLM ID: 101563288 Publication Model: Electronic Cited Medium: Internet ISSN:

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Academic Journal

A horizontal and perpendicular interlaminar approach for intrathecal nusinersen injection in patients with spinal muscular atrophy and scoliosis: an observational study.

  • Authors : Huang C; Department of Anesthesiology, The First Affiliated Hospital, Sun Yat-Sen University, Guangzhou, China.; Zhang Y

Subjects: Scoliosis*/Scoliosis*/Scoliosis*/drug therapy ; Scoliosis*/Scoliosis*/Scoliosis*/diagnostic imaging ; Muscular Atrophy, Spinal*/Muscular Atrophy, Spinal*/Muscular Atrophy, Spinal*/drug therapy

  • Source: Orphanet journal of rare diseases [Orphanet J Rare Dis] 2024 Jul 15; Vol. 19 (1), pp. 268. Date of Electronic Publication: 2024 Jul 15.Publisher: BioMed Central Country of Publication: England NLM ID: 101266602 Publication Model: Electronic Cited Medium: Internet ISSN: 1750-1172

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Academic Journal

Population pharmacokinetics of imetelstat, a first-in-class oligonucleotide telomerase inhibitor.

  • Authors : González-Sales M; Modeling Great Solutions Pharmaceutical Research & Studies, FZE, Dubai, United Arab Emirates.; Lennox AL

Subjects: Telomerase*/Telomerase*/Telomerase*/antagonists & inhibitors ; Oligonucleotides*/Oligonucleotides*/Oligonucleotides*/pharmacokinetics ; Oligonucleotides*/Oligonucleotides*/Oligonucleotides*/administration & dosage

  • Source: CPT: pharmacometrics & systems pharmacology [CPT Pharmacometrics Syst Pharmacol] 2024 Jul; Vol. 13 (7), pp. 1264-1277. Date of Electronic Publication: 2024 May 21.Publisher: Wiley Country of Publication: United States NLM ID: 101580011 Publication Model: Print-Electronic Cited Medium: Internet ISSN:

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Academic Journal

Analysis of the efficacy and adverse effects of nusinersen in the treatment of children with spinal muscular atrophy in China.

  • Authors : Li D; Department of Pediatrics, The Second Affiliated Hospital of Xi'an Jiaotong University, Xi'an, Shaanxi, China.; Yang J

Subjects: Oligonucleotides*/Oligonucleotides*/Oligonucleotides*/adverse effects ; Oligonucleotides*/Oligonucleotides*/Oligonucleotides*/administration & dosage ; Oligonucleotides*/Oligonucleotides*/Oligonucleotides*/pharmacology

  • Source: Brain and behavior [Brain Behav] 2024 Jul; Vol. 14 (7), pp. e3630.Publisher: John Wiley & Sons Country of Publication: United States NLM ID: 101570837 Publication Model: Print Cited Medium: Internet ISSN:

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Academic Journal

Trivalent Disulfide Unit-Masked System Efficiently Delivers Large Oligonucleotide.

  • Authors : Wang L; School of Pharmacy, Jiangsu Province Key Laboratory for Inflammation and Molecular Drug Target, Nantong University, Nantong 226001, China.; Liu X

Subjects: Disulfides*/Disulfides*/Disulfides*/chemistry ; Oligonucleotides*/Oligonucleotides*/Oligonucleotides*/chemistry; Animals

  • Source: Molecules (Basel, Switzerland) [Molecules] 2024 Sep 05; Vol. 29 (17). Date of Electronic Publication: 2024 Sep 05.Publisher: MDPI Country of Publication: Switzerland NLM ID: 100964009 Publication Model: Electronic Cited Medium: Internet ISSN: 1420-3049

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Academic Journal

Pulsed Dipolar EPR for Self-Limited Complexes of Oligonucleotides Studies.

  • Authors : Chubarov AS; Institute of Chemical Biology and Fundamental Medicine SB RAS, 630090 Novosibirsk, Russia.; Endeward B

Subjects: Molecular Dynamics Simulation* ; Oligonucleotides*/Oligonucleotides*/Oligonucleotides*/chemistry ; Spin Labels*

  • Source: Biomolecules [Biomolecules] 2024 Jul 23; Vol. 14 (8). Date of Electronic Publication: 2024 Jul 23.Publisher: MDPI Country of Publication: Switzerland NLM ID: 101596414 Publication Model: Electronic Cited Medium: Internet ISSN: 2218-273X

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Academic Journal

An autocatalytic CRISPR-Cas amplification effect propelled by the LNA-modified split activators for DNA sensing.

  • Authors : Sun K; Department of Laboratory Medicine, State Key Laboratory of Biotherapy and Clinical Laboratory Medicine Research Center, West China Hospital, Sichuan University, Chengdu, 610041 Chengdu, China.; Tianfu Jincheng Laboratory, City of Future Medicine, Chengdu 641400, China.

Subjects: CRISPR-Cas Systems* ; Oligonucleotides*/Oligonucleotides*/Oligonucleotides*/chemistry ; Oligonucleotides*/Oligonucleotides*/Oligonucleotides*/genetics

  • Source: Nucleic acids research [Nucleic Acids Res] 2024 Apr 24; Vol. 52 (7), pp. e39.Publisher: Oxford University Press Country of Publication: England NLM ID: 0411011 Publication Model: Print Cited Medium: Internet ISSN:

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Academic Journal

Modern approaches to therapeutic oligonucleotide manufacturing.

  • Authors : Obexer R; Manchester Institute of Biotechnology, Department of Chemistry, University of Manchester, Manchester, UK.; Nassir M

Subjects: Oligonucleotides*/Oligonucleotides*/Oligonucleotides*/chemical synthesis ; Oligonucleotides*/Oligonucleotides*/Oligonucleotides*/therapeutic use; Chemistry Techniques, Synthetic

  • Source: Science (New York, N.Y.) [Science] 2024 Apr 12; Vol. 384 (6692), pp. eadl4015. Date of Electronic Publication: 2024 Apr 12.Publisher: American Association for the Advancement of Science Country of Publication: United States NLM ID: 0404511 Publication Model: Print-Electronic

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