نتائج البحث

Phase 3 trial of RNAi therapeutic givosiran for acute intermittent porphyria

• Authors : Balwani, M.; Sardh, E.; Ventura, P.

• Source: Balwani , M , Sardh , E , Ventura , P , Peiró , P A , Rees , D C , Stölzel , U , Bissell , D M , Bonkovsky , H L , Windyga , J , Anderson , K E , Parker , C , Silver , S M , Keel , S B , Wang , J D

تفاصيل العنوان

Phase 3 trial of RNAi therapeutic givosiran for acute intermittent porphyria

• Authors : Balwani, M.; Sardh, E.; Ventura, P.

• Source: Balwani , M , Sardh , E , Ventura , P , Peiró , P A , Rees , D C , Stölzel , U , Bissell , D M , Bonkovsky , H L , Windyga , J , Anderson , K E , Parker , C , Silver , S M , Keel , S B , Wang , J D

تفاصيل العنوان

EXPLORE:A Prospective, Multinational, Natural History Study of Patients with Acute Hepatic Porphyria with Recurrent Attacks

• Authors : Gouya, Laurent; Ventura, Paolo; Balwani, Manisha

• Source: Gouya , L , Ventura , P , Balwani , M , Bissell , D M , Rees , D C , Stölzel , U , Phillips , J D , Kauppinen , R , Langendonk , J G , Desnick , R J , Deybach , J C , Bonkovsky , H L , Parker , C ,

تفاصيل العنوان

Phase 1 Trial of an RNA Interference Therapy for Acute Intermittent Porphyria

• Authors : Sardh, Eliane; Harper, Pauline; Balwani, Manisha

Subjects: Adult; Dose-Response Relationship; Drug

• Source: Sardh , E , Harper , P , Balwani , M , Stein , P , Rees , D C , Bissell , D M , Desnick , R , Parker , C , Phillips , J , Bonkovsky , H L , Vassiliou , D , Penz , C , Chan-Daniels , A , He , Q ,

تفاصيل العنوان

EXPLORE:A Prospective, Multinational, Natural History Study of Patients with Acute Hepatic Porphyria with Recurrent Attacks

• Authors : Gouya, Laurent; Ventura, Paolo; Balwani, Manisha

• Source: Gouya , L , Ventura , P , Balwani , M , Bissell , D M , Rees , D C , Stölzel , U , Phillips , J D , Kauppinen , R , Langendonk , J G , Desnick , R J , Deybach , J C , Bonkovsky , H L , Parker , C ,

تفاصيل العنوان

Phase 1 Trial of an RNA Interference Therapy for Acute Intermittent Porphyria

• Authors : Sardh, Eliane; Harper, Pauline; Balwani, Manisha

Subjects: Adult; Dose-Response Relationship; Drug

• Source: Sardh , E , Harper , P , Balwani , M , Stein , P , Rees , D C , Bissell , D M , Desnick , R , Parker , C , Phillips , J , Bonkovsky , H L , Vassiliou , D , Penz , C , Chan-Daniels , A , He , Q ,

تفاصيل العنوان