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Emerging treatments for Retinitis Pigmentosa

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  • معلومة اضافية
    • بيانات النشر:
      University of Malta. Department of Pharmacy
    • الموضوع:
      2021
    • Collection:
      University of Malta: OAR@UM / L-Università ta' Malta
    • نبذة مختصرة :
      Retinitis Pigmentosa (RP) is a class of rare-inherited retinal dystrophies which can lead to blindness and is characterised by pigment deposits predominantly present in the periphery of the retina. The hereditary pattern of RP follows a Mendelian inheritance pattern. The onset of RP typically occurs during the early teenage years with difficulties in dark adaptation, concurrent nyctalopia and reduced visual field (VF) which leads to tunnel vision and gradual reduction in central vision with a risk of blindness. Currently, no standard treatment for RP is available. One medicinal product (MP), Luxturna, which consists of voretigene neparvovec, a gene transfer vector, is authorised in the European Union (EU) and United States (US) to treat patients with inherited retinal dystrophies, caused by biallelic RPE65 mutations, and who have sufficient viable retinal cells. ; N/A
    • Relation:
      Zuccarelli, M., Borg, J. J., Vella Szijj, J., Azzopardi, L. M., & Serracino-Inglott, A. (2021). Emerging treatments for Retinitis Pigmentosa. 12th World Meeting on Pharmaceutics, Biopharmaceutics and Pharmaceutical Technology.; https://www.um.edu.mt/library/oar/handle/123456789/77247
    • الدخول الالكتروني :
      https://www.um.edu.mt/library/oar/handle/123456789/77247
    • Rights:
      info:eu-repo/semantics/openAccess ; The copyright of this work belongs to the author(s)/publisher. The rights of this work are as defined by the appropriate Copyright Legislation or as modified by any successive legislation. Users may access this work and can make use of the information contained in accordance with the Copyright Legislation provided that the author must be properly acknowledged. Further distribution or reproduction in any format is prohibited without the prior permission of the copyright holder.
    • الرقم المعرف:
      edsbas.4488AB25