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Academic Journal

Efficacy and safety of thalidomide in children with monogenic autoinflammatory diseases: a single-center, real-world-evidence study.

  • Authors : Zhang C; Department of Pediatrics, Peking Union Medical College Hospital, Chinese Academy of Medical Sciences & Peking Union Medical College, No. 1 Shuaifuyuan Wangfujing Dongcheng District, Beijing, 100730, China.; Yu Z

Subjects: Hereditary Autoinflammatory Diseases*/Hereditary Autoinflammatory Diseases*/Hereditary Autoinflammatory Diseases*/drug therapy ; Hereditary Autoinflammatory Diseases*/Hereditary Autoinflammatory Diseases*/Hereditary Autoinflammatory Diseases*/genetics ; Familial Mediterranean Fever*/Familial Mediterranean Fever*/Familial Mediterranean Fever*/drug therapy Periodic fever, familial, autosomal dominant

  • Source: Pediatric rheumatology online journal [Pediatr Rheumatol Online J] 2023 Oct 17; Vol. 21 (1), pp. 124. Date of Electronic Publication: 2023 Oct 17.Publisher: BioMed Central Country of Publication: England NLM ID: 101248897 Publication Model: Electronic Cited Medium: Internet ISSN: 1546-0096

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  • 1-2 ل  2 نتائج ل ""A20 haploinsufficiency""