نتائج البحث

New Imaging Biomarkers for Muscular Diseases - Multispectral Optoacoustic Imaging in Spinal Muscular Atrophy (MSOT_SMA)

• Source: New Imaging Biomarkers for Muscular Diseases - Multispectral Optoacoustic Imaging in Spinal Muscular

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An MRI Study on Muscular Diseases -Pompe Disease and Dystrophia Myotonica

• Source: Function, Structure and Quality of Striated Muscles in Patients With Muscular Diseases - an MRI Study on Pompe Disease and Dystrophia

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Quantitative Muscle Ultrasound as a Marker of Progression in Children With Muscular Diseases

• Authors : Waleed Ahmed Salaheldeen Hassan, Assistant professor

• Source: Quantitative Muscle Ultrasound as a Monitoring Tool of Disease Progression in Children With Inflammatory Myositis and Duchenne Muscular Dystrophy

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Study of Inherited Neurological Disorders

• Source: Clinical and Molecular Manifestations of Inherited Neurological Disorders

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NKX019, Intravenous Allogeneic Chimeric Antigen Receptor Natural Killer Cells (CAR NK), in Participants With Immune-Mediated Diseases (Ntrust-2)

• Source: A Phase 1 Study of NKX019, a CD19 Chimeric Antigen Receptor Natural Killer (CAR NK) Cell Therapy, in Subjects With Immune-Mediated Diseases

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A Natural History Study of Patients With GNE Myopathy and GNE-Related Diseases

• Authors : Therapeutics for Rare and Neglected Diseases (TRND)

• Source: A Natural History Study of Patients With GNE Myopathy and GNE-Related DiseasesLiu CY, Yao J, Kovacs WC, Shrader JA, Joe G, Ouwerkerk R, Mankodi AK, Gahl WA,

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RESET-Myositis: An Open-Label Study to Evaluate the Safety and Efficacy of CABA-201 in Subjects With Active Idiopathic Inflammatory Myopathy or Juvenile Idiopathic Inflammatory Myopathy

• Source: A Phase 1/2, Open-Label Study to Evaluate the Safety and Efficacy of Autologous CD19-specific Chimeric Antigen Receptor T Cells (CABA-201) in Subjects With Active Idiopathic Inflammatory Myopathy or

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A Study of CC-97540, CD-19-Targeted Nex-T CAR T Cells, in Participants With Severe, Refractory Autoimmune Diseases (Breakfree-1)

• Authors : Bristol-Myers Squibb Services Unlimited Company

• Source: A Phase 1, Multicenter, Open-Label Study Of CC-97540 (BMS-986353), CD19-Targeted Nex-T Chimeric Antigen Receptor (CAR) T Cells, in Participants With Severe, Refractory Autoimmune

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A Safety and Efficacy Study Evaluating CTX112 in Adult Subjects With Refractory Autoimmune Disease

• Source: A Phase 1 Dose Evaluation Study of the Safety and Preliminary Efficacy of Anti-CD19 Allogeneic CRISPR-Cas9-Engineered T Cells (CTX112) in Adult Subjects With Refractory Autoimmune Disease

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Genetic and Physical Study of Childhood Nerve and Muscle Disorders

• Source: Clinical and Molecular Manifestations of Neuromuscular and Neurogenetic Disorders of Childhood

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