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Gene editing of hematopoietic stem cells restores T cell response in familial hemophagocytic lymphohistiocytosis

• Authors : Dettmer‐Monaco, Viviane; Weissert, Kristoffer; Ammann, Sandra

• Source: The journal of allergy and clinical immunology. - 153, 1 (2024) , 243-255.e14, ISSN: 1097-6825

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Gene editing of NCF1 loci is associated with homologous recombination and chromosomal rearrangements

• Authors : Raimondi, Federica; Siow, Kah Mun; Wrona, Dominik

• Source: Communications biology. - 7, 1 (2024) , 1291, ISSN: 2399-3642

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Progress and harmonization of gene editing to treat human diseases: Proceeding of COST Action CA21113 GenE-HumDi

• Authors : Cavazza, Alessia; Hendel, Ayal; Bak, Rasmus O.

• Source: Molecular therapy. Nucleic acids. - 34 (2023) , 102066, ISSN: 2162-2531

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CRISPR-Cas9 based gene editing of the immune checkpoint NKG2A enhances NK cell mediated cytotoxicity against multiple myeloma

• Authors : Bexte, Tobias; Alzubi, Jamal; Reindl, Lisa Marie

• Source: OncoImmunology. - 11, 1 (2022) , 2081415, ISSN: 2162-402X

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Chimeric oligonucleotides combining guide RNA and single-stranded DNA repair template effectively induce precision gene editing

• Authors : Ghosh, Avantika; Myacheva, Ksenia; Riester, Marisa

• Source: RNA biology. - 19, 1 (2022) , 588-593, ISSN: 1555-8584

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TALEN mediated gene editing in a mouse model of Fanconi anemia

• Authors : Pino-Barrio, Maria José; Giménez, Yari; Villanueva, Mariela

• Source: Scientific reports. - 10, 1 (2020) , 6997, ISSN: 2045-2322

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Hijacking-DNA -Repair (HDR)-CRISPR promotes seamless gene editing in human primary cells

• Authors : Carusillo, Antonio

Subjects: CRISPR/Cas-Methode

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Editing the core region in HPFH deletions alters fetal and adult globin expression for treatment of [beta]-hemoglobinopathies

• Authors : Venkatesan, Vigneshwaran; Rhiel, Manuel; Andrieux, Geoffroy

• Source: Molecular therapy. Nucleic acids. - 32 (2023) , 671-688, ISSN: 2162-2531

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Genome editing with TALEN, CRISPR-Cas9 and CRISPR-Cas12a in combination with AAV6 homology donor restores T cell function for XLP

• Authors : Houghton, Benjamin C.; Panchal, Neelam; Haas, Simone

• Source: Frontiers in genome editing. - 4 (2022) , 828489, ISSN: 2673-3439

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A non-viral and selection-free COL7A1 HDR approach with improved safety profile for dystrophic epidermolysis bullosa

• Authors : Kocher, Thomas; Bischof, Johannes; Haas, Simone

• Source: Molecular therapy. Nucleic acids. - 25 (2021) , 237-250, ISSN: 2162-2531

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