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Intracerebroventricular administration of a modified hexosaminidase ameliorates late-stage neurodegeneration in a GM2 mouse model.
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- المؤلفون: Lopez, Manuel E.1 (AUTHOR) ; Wendt, Daniel1 (AUTHOR); Lawrence, Roger1 (AUTHOR); Gong, Kerui1 (AUTHOR); Ong, Hoonsan1 (AUTHOR); Yip, Bryan1 (AUTHOR); Chen, Joseph1 (AUTHOR); Mangini, Linley1 (AUTHOR); Handyside, Britta1 (AUTHOR); Giaramita, Alexander1 (AUTHOR); Lamichhane, Aashish1 (AUTHOR); Lo, Melanie1 (AUTHOR); Agrawal, Vishal1 (AUTHOR); Van Vleet, Jeremy1 (AUTHOR); Abolhesn, Amanda1 (AUTHOR); Felix, Jessica B.1 (AUTHOR); Villalpando, Isaac1 (AUTHOR); Bhat, Vikas1 (AUTHOR); De Angelis, Rolando1 (AUTHOR); Ru, Yuanbin1 (AUTHOR)
- المصدر:
PLoS ONE. 1/3/2025, Vol. 20 Issue 1, p1-19. 19p.
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